Spinal muscular atrophy patients’ walking distance improved after Nusinersen treatment
A positive effect of nusinersen treatment on motor function in ambulant pediatric and adult spinal muscular atrophy (SMA) patients during…
A positive effect of nusinersen treatment on motor function in ambulant pediatric and adult spinal muscular atrophy (SMA) patients during…
Adopting some of the strategies behind successfully treating the childhood disease spinal muscular atrophy may enable development of therapies to…